Researchers plan to begin the first patient trial in 2027 thanks to promising preclinical results from a gene therapy ...

With promise to slow aging and cure some types of cancer, a new gene therapy presents cost and access hurdles for CT patients ...

An expert involved in the first successful gene therapy trial for Huntington's Disease discusses the trial results and ...

The Barbara Ann Karmanos Cancer Institute in Detroit has become the first and only independent cancer center in the U.S. to ...

Karmanos 1st debut novel gene therapy offers a one-time treatment for adult hemophilia B, reducing the need for routine factor IX infusions.

Etranacogene dezaparvovec (Hemgenix), the only commercially available gene therapy for hemophilia B, is temporarily ...

Eli Lilly and Regeneron are leading the push to treat congenital deafness with gene therapies, seeking a piece of a potential ...

Global stockout halts access to Hemgenix gene therapy, delaying treatment for adults with hemophilia B amid manufacturing ...

A genetic variant carried by at least one-fifth of the population may do far more than raise the odds of developing Alzheimer ...

Nemours Children's Hospital is now offering Lyfgenia gene therapy. The treatment aims to reduce pain crises and hospital visits for young patients.

OCGN's gene-agnostic eye therapy aims to treat multiple retinal mutations, with key filings and pivotal data in 2026???2027 set to test its broad platform.

The last available hemophilia gene therapy is temporarily unavailable, according to CSL Behring.  | The company is working ...